Anna Ericsson,Neal Green,Gary Gustafson,David R. Lancia, JR.,Gary Marshall,Lorna Mitchell,David Richard,Zhongguo Wang,Forsyth Sanjeev,Kelly J. Patrick,Madhu Mondal,Maria Ribadeneira,Schroeder Patricia
申请号：
US16576720
公开号：
US20200129485A1
申请日:
2019.09.19
申请国别(地区):
US
年份:
2020
代理人:
摘要：
Compounds that activate pyruvate kinase R can be used for the treatment of sickle cell disease (SCD). Methods and compositions for the treatment of SCD are provided herein, including a therapeutic compound designated as Compound 1.
