Sestavki za moduliranje izražanja C9ORF72
- 专利权人:
- Ionis Pharmaceuticals; Inc.
- 发明人:
- RIGO Frank
- 申请号：
- SI201630693
- 公开号：
- SI3283080T1
- 申请日:
- 2016.04.15
- 申请国别(地区):
- SI
- 年份:
- 2020
- 代理人:
- 摘要：
- Disclosed herein are compositions and methods for reducing expression of C9ORF72 mRNA and protein in an animal. Such methods are useful to treat, prevent, ameliorate, or slow progression of neurodegenerative diseases in an individual in need thereof.
- 来源网站：
- 中国工程科技知识中心
