Fred Hutchinson Cancer Research Center;Seattle Children's Hospital d/b/a Seattle Children's Research Institute
发明人:
Frieda Chan,Olivier Humbert,Hans-Peter Kiem,Jennifer E. Adair,David Rawlings,Andrew Scharenberg,Troy Torgerson
申请号:
US16486442
公开号:
US20200009266A1
申请日:
2018.02.15
申请国别(地区):
US
年份:
2020
代理人:
摘要:
In vivo gene therapies for immune deficiencies are described. The in vivo gene therapies utilize a foamy viral vector including a PGK promoter with a therapeutic gene. The foamy viral vector can be beneficially administered with cell mobilization into the peripheral blood.