VECTORS WITH PROMOTER AND ENHANCER COMBINATIONS FOR TREATING PHENYLKETONURIA

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专利权人:

American Gene Technologies International Inc.

发明人:

Tyler Lahusen,Charles David Pauza

申请号：

US16652867

公开号：

US20200318081A1

申请日:

2018.10.02

申请国别(地区):

US

年份:

2020

代理人:

摘要：

A lentiviral vector system for expressing a lentiviral particle is disclosed. The lentiviral vector system includes a therapeutic vector. The lentiviral vector system produces a lentiviral particle for upregulating PAH expression in the cells of a subject afflicted with phenylketonuria (PKU).

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/