OPPENHEIMER DANIEL I,KAKKIS EMIL D.,PRICE FREDRIC D.,DORENBAUM ALEJANDRO
申请号：
PL04819152
公开号：
PL1708690T3
申请日:
2004.11.17
申请国别(地区):
PL
年份:
2017
代理人:
摘要：
The present invention is directed to a novel methods and compositions for the therapeutic intervention in hyperphenylalaninemia. More specifically, the specification describes methods and compositions for treating various types of phenylketonurias using compositions comprising BH4. Combination therapies of BH4 and other therapeutic regimens are contemplated.
