Tsafi Pe'ery;Tsafi Peery;Michael B. Mathews;Mainul Hoque;Hartmut M. Hanauske-Abel
发明人:
Tsafi Pe'ery,Michael B. Mathews,Mainul Hoque,Hartmut M. Hanauske-Abel,Tsafi Peery
申请号：
US14126342
公开号：
US09849146B2
申请日:
2012.06.13
申请国别(地区):
US
年份:
2017
代理人:
摘要：
Provided are methods for treating a NAD comprising administering to a patient suffering from a NAD an inhibitor of NMD and a nonsense suppressor, whereby degradation of NMD susceptible mRNA is decreased and translation termination at a misplaced nonsense codon is blocked.
