THE CHILDREN'S HOSPITAL OF PHILADELPHIA;THE CHILDRENS HOSPITAL OF PHILADELPHIA
发明人:
DAVIDSON, BEVERLY L.,MONTEYS, ALEJANDRO MAS,KEISER, MEGAN S.
申请号:
CA3018076
公开号:
CA3018076A1
申请日:
2017.03.17
申请国别(地区):
CA
年份:
2017
代理人:
摘要:
The present disclosure provides filler or stuffer sequences, compositions thereof including expression cassettes and vectors, such as viral (e.g., AAV) vectors and methods of delivering a therapeutic agent to a mammal and/or treating a disease.