Research Institute at Nation Wide Children's Hospital
发明人:
Harper, Scott Quenton
申请号:
AU20170240236
公开号:
AU2017240236(A1)
申请日:
2017.03.31
申请国别(地区):
澳大利亚
年份:
2018
代理人:
摘要:
The present invention relates to a tissue-specific promoter system for expressing microRNA (miRNA) for RNA interference-based methods of gene therapy. In these systems, the miRNA will inhibit gene expression or replace natural miRNA expression using microRNA.