promoter for cell - specific gene expression and uses thereof

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专利权人:

UNIVERSITA' DEL PIEMONTE ORIENTALE;UNIVERSITA DEL PIEMONTE ORIENTALE

发明人:

FOLLENZI, ANTONIA,ZANOLINI, DIEGO,FAMA', ROSELLA,MERLIN, SIMONE,FOLLENZI ANTONIA,ZANOLINI DIEGO,FAMA, ROSELLA,FAMA ROSELLA,MERLIN SIMONE

申请号：

ITUA20164289

公开号：

ITUA20164289A1

申请日:

2016.06.10

申请国别(地区):

IT

年份:

2017

代理人:

摘要：

The present invention refers to nucleotide sequences used for driving the expression of a therapeutic gene, preferably FVIII and/or its variants specifically in endothelial cells and/or hematopoietic, preferably myeloid cells. The sequences are useful for gene and/or cell therapy, preferably for treating hemophilia, more preferably type A hemophilia.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/