CHATTERJEE, SASWATI,WONG, KAMEHAMEHA K.,BENHAJSALAH, MARWA,SMITH, LAURA JANE,SEYMOUR, ALBERT BARNES,WRIGHT, JASON BOKE,MCSWIGGEN, JAMES ANTHONY,DOLLIVE, SERENA NICOLE,ST. MARTIN, THIA BABOVAL,PROUT, J
申请号：
CA3079437
公开号：
CA3079437A1
申请日:
2018.10.17
申请国别(地区):
CA
年份:
2019
代理人:
摘要：
Provided herein are adeno-associated virus (AAV) compositions for correcting a mutation in a beta globin gene (HBB) gene and methods of using the same to correct an HBB gene mutation in a cell. Also provided are packaging systems for making the adeno-associated virus compositions.
