Swayze, Eric E.,Cole, Tracy,Kordasiewicz, Holly,Freier, Susan M.,Condon, Thomas P.,Wancewicz, Edward,Lockhart, Trisha,Vickers, Timothy,Singh, Priyam
申请号:
AU2019268063
公开号:
AU2019268063A1
申请日:
2019.11.19
申请国别(地区):
AU
年份:
2019
代理人:
摘要:
#$%^&*AU2019268063A120191212.pdf#####ABSTRACT Disclosed herein are antisense compounds and methods for decreasing SOD-1 mRNA and protein expression. Such methods, compounds, and compositions are useful to treat, prevent, or ameliorate SOD-1 associated diseases, disorders, and conditions. Such SOD-1 associated diseases include amyotrophic sclerosis (ALS).