William Querbes,Kevin Fitzgerald,Brian Bettencourt,Abigail Liebow,David V. Erbe
申请号：
US16673863
公开号：
US20200316201A1
申请日:
2019.11.04
申请国别(地区):
US
年份:
2020
代理人:
摘要：
The invention relates to RNAi agents, e.g., double-stranded RNAi agents, targeting the HAO1 gene, and methods of using such RNAi agents to inhibit expression of HAO1 and methods of treating subjects having, e.g., PH1.
