Ospedale San Raffaele S.r.l.;Children's Medical Center Corporation;Dana-Farber Cancer Institute, Inc.
发明人:
Biffi, Alessandra,Cavalca, Eleonora
申请号:
AU2018210853
公开号:
AU2018210853A1
申请日:
2018.01.16
申请国别(地区):
AU
年份:
2019
代理人:
摘要:
The present invention provides compositions and methods for the treatment or prevention of a lysosomal disease or disorder involving increasing the level, expression, or activity of a metallothionein polypeptide or polynucleotide in the subject.