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THE USE OF DEFERIPRONE AND METHODS TO TREAT AND/OR PREVENT FRIEDREICH ATAXIA RESULTING FROM INTRACELLULAR MISHANDLING OF IRON
专利权人:
MUNNICH, ARNOLD;SPINO, MICHAEL;CABANTCHIK, IOAV
发明人:
MUNNICH, ARNOLD,SPINO, MICHAEL,CABANTCHIK, IOAV
申请号:
MYPI 20083186
公开号:
MY151412A
申请日:
2007.02.21
申请国别(地区):
MY
年份:
2014
代理人:
摘要:
A THERAPEUTICALLY EFFECTIVE AMOUNT OF DEFERIPRONE OR DEFERASIROX OR PHYSIOLOGICALLY ACCEPTABLE SALTS THEREOF FOR THE PREVENTION, STABILIZATION, TREATMENT, OR REVERSAL OF IRON-INDUCED FRDA DISEASE IN PATIENTS RESULTING FROM MITOCHONDRIAL IRON-INDUCED DAMAGE TO PREFERENTIALLY REDUCE THE IRON STORES IN THE MITOCHONDRIA. ALSO FOR THE TREATMENT OF OTHER CONDITIONS AFFECTING THE BRAIN WHERE A KEY ELEMENT IN THE GENERATION OF THE RESULTANT PATHOLOGY IS THE INTRACELLULAR MISHANDLING OF IRON.
来源网站:
中国工程科技知识中心
来源网址:
http://www.ckcest.cn/home/

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