COLD SPRING HARBOR LABORATORY;Stoke Therapeutics, Inc.
发明人:
申请号:
EP16876615.2
公开号:
EP3390635A4
申请日:
2016.12.14
申请国别(地区):
EP
年份:
2019
代理人:
摘要:
Provided herein are methods and compositions for increasing the expression of TSC2, and for treating a subject in need thereof, such as a subject with deficient tuberin protein expression or a subject having tuberous sclerosis complex.