The United States of America; as represented by the Secretary; Department of Health and Human Services
发明人:
VENDITTI, Charles,PAVAN, William,CHANDLER, Randy
申请号：
ES16717228
公开号：
ES2755725T3
申请日:
2016.04.07
申请国别(地区):
ES
年份:
2020
代理人:
摘要：
Nucleic acid construct comprising: (1) a viral vector； and (2) an NPC1 gene sequence under the control of an elongation factor 1 α (EF1α) promoter, where optionally the EF1a promoter comprises SEQ ID NO: 8.Constructo de ácido nucleico que comprende: (1) un vector viral； y (2) una secuencia de gen NPC1 bajo el control de un promotor del factor de elongación 1 α (EF1α), en el que opcionalmente el promotor del EF1a comprende SEQ ID NO: 8.
