Alfica Sehgal,Klaus Charisse,Brian Bettencourt,Martin A. Maier,Kallanthottathil G. Rajeev,Gregory Hinkle,Muthiah Manoharan
申请号：
US16679691
公开号：
US20200080085A1
申请日:
2019.11.11
申请国别(地区):
US
年份:
2020
代理人:
摘要：
The invention relates to RNAi agents, e.g., double-stranded RNAi agents, targeting the Serpina1 gene, and methods of using such RNAi agents to inhibit expression of Serpina1 and methods of treating subjects having a Serpina1 associated disease, such as a liver disorder.
