COLD SPRING HARBOR LABORATORY;STOKE THERAPEUTICS, INC.
发明人:
AZNAREZ, ISABEL,NASH, HUW M.,KRAINER, ADRIAN
申请号:
CA3005249
公开号:
CA3005249A1
申请日:
2016.12.14
申请国别(地区):
CA
年份:
2017
代理人:
摘要:
Provided herein are methods and compositions for increasing the expression of a protein, and for treating a subject in need thereof, e.g., a subject with deficient protein expression or a subject having a kidney disease.