SERPINA1-IRNA COMPOSITIONS AND PROCEDURES FOR USE THEREOF

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专利权人:

Alnylam Pharmaceuticals; Inc.

发明人:

SEHGAL, Alfica,CHARISSE, Klaus,BETTENCOURT, Brian,MAIER, Martin,RAJEEV, Kallanthottathil G.,HINKLE, Gregory,MANOHARAN, Muthiah

申请号：

DK14730051

公开号：

DK2999785T3

申请日:

2014.05.22

申请国别(地区):

DK

年份:

2018

代理人:

摘要：

The invention relates to RNAi agents, e.g., double-stranded RNAi agents, targeting the Serpina1 gene, and methods of using such RNAi agents to inhibit expression of Serpina1 and methods of treating subjects having a Serpina1 associated disease, such as a liver disorder.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/