DODGE, JAMES,PASSINI, MARCO A.,SHIHABUDDIN, LAMYA,CHENG, SENG H.
申请号：
CA2636991
公开号：
CA2636991C
申请日:
2007.01.22
申请国别(地区):
CA
年份:
2017
代理人:
摘要：
Lysosomal storage diseases can be successfully treated using intraventriculardelivery of the enzyme which is etiologically deficient in the disease. Theadministration can be performed slowly to achieve maximum effect.Surprisingly, effects are seen on both sides of the blood- brain barrier,making this an ideal delivery means for lysosomal storage diseases whichaffect both brain and visceral organs.
