AUGMENTED ACID ALPHA-GLUCOSIDASE FOR THE TREATMENT OF POMPE DISEASE

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专利权人:

发明人:

DO HUNG V,KHANNA RICHIE,GOTSCHALL RUSSELL

申请号：

IN201847027738

公开号：

IN201847027738A

申请日:

2018.07.24

申请国别(地区):

IN

年份:

2018

代理人:

摘要：

A method for treating Pompe disease including administration of recombinant human acid a-glucosidase having optimal glycosylation with mannose-6-phosphate residues in combination with an amount of miglustat effective to maximize tissue uptake of recombinant human acid a-glucosidase while minimizing inhibition of the enzymatic activity of the recombinant human acid a-glucosidase is provided.

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中国工程科技知识中心

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