RAAV-based compositions and methods
- 专利权人:
- University of Massachusetts
- 发明人:
- Terence Flotte,Christian Mueller,Phillip D. Zamore
- 申请号：
- US16059121
- 公开号：
- US10597656B2
- 申请日:
- 2018.08.09
- 申请国别(地区):
- US
- 年份:
- 2020
- 代理人:
- 摘要：
- The invention relates to isolated nucleic acids and rAAV-based compositions, methods and kits useful for treating genetic diseases (e.g., alpha-1 antitrypsin deficiency).
- 来源网站：
- 中国工程科技知识中心
