SEHGAL, ALFICA,SIGOVA, ALLA A.,ZLOBINE, IGOR,SCHWARTZ, BRIAN E.,BUMCROT, DAVID A.
申请号:
CA3078247
公开号:
CA3078247A1
申请日:
2018.10.09
申请国别(地区):
CA
年份:
2019
代理人:
摘要:
The present invention provides methods and compositions for the treating a patient with a urea cycle disorder. Methods and compositions are also provided for modulating genes encoding enzymes that participate in the urea cycle by altering gene signaling networks.