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MATERIALS AND METHODS FOR PREVENTION OF MUSCLE DISEASES
专利权人:
BIOMARIN TECHNOLOGIES B.V.;ACADEMISCH ZIEKENHUIS LEIDEN
发明人:
VAN DEUTEKOM, JUDITH CHRISTINA THEODORA,AARTSMA-RUS, ANNEMIEKE,VAN OMMEN, GARRIT-JAN, BOUDEWIJN,PLATENBURG, GERARDUS JOHANNES,DE KIMPE, JOSEPHUS, JOHANNES
申请号:
DK08842559
公开号:
DK2203173T3
申请日:
2008.10.27
申请国别(地区):
DK
年份:
2016
代理人:
摘要:
The invention provides means and methods for alleviating one or more symptom(s) of Duchenne Muscular Dystrophy and/or Becker Muscular Dystrophy. Therapies using compounds for providing patients with functional muscle proteins are combined with at least one adjunct compound for reducing inflammation, preferably for reducing muscle tissue inflammation, and/or at least one adjunct compound for improving muscle fiber function, integrity and/or survival.
来源网站:
中国工程科技知识中心
来源网址:
http://www.ckcest.cn/home/

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