compound, modified oligonucleotide, pharmaceutical composition, method for inhibiting the activity of one or more mir-17 family members in a cell and in a subject
Methods for treating polycystic kidney disease, including autosomal dominant polycystic kidney disease, using mir-17-directed modified oligonucleotides are provided herein.são fornecidos neste documento métodos para o tratamento de doença renal policística, incluindo doença renal policística dominante autossômica, usando oligonucleotídeos modificados direcionados para mir-17.