THE REGENTS OF THE UNIVERSITY OF MICHIGAN;UCL BUSINESS LTD
发明人:
THOMPSON, Debra A.,ALI, Robin R.,SMITH, Alexander J.
申请号：
SG11202004527Y
公开号：
SG11202004527YA
申请日:
2018.11.15
申请国别(地区):
SG
年份:
2020
代理人:
摘要：
Provided are materials, methods and uses for treating an ophthalmological condition such as Leber Congenital Amaurosis by administering an effective amount of an adeno-associated virus AAV2, serotype 5 (AAV 2/5) or AAV-5 comprising an expressible coding region for human RDH12.
