methods and compositions to modulate splicing

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专利权人:

SKYHAWK THERAPEUTICS; INC.

发明人:

KATHLEEN MCCARTHY,MICHAEL LUZZIO,WILLIAM HANEY

申请号：

BR112020002270

公开号：

BR112020002270A2

申请日:

2018.08.03

申请国别(地区):

BR

年份:

2020

代理人:

摘要：

described here are small molecule splicing modulating compounds that modulate mrna splicing, such as pre-mrna, encoded by genes, and methods of using small molecule splicing modulating compounds to modulate splicing and treat diseases and conditions .são descritos no presente documento compostos moduladores de splicing de molécula pequena que modulam o splicing de mrna, tal como pré-mrna, codificado por genes, e métodos de uso dos compostos moduladores de splicing de molécula pequena para modular o splicing e tratar doenças e condições.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/