SUHY, David,GRAHAM, Michael,TROLLET, Capucine,MALERBA, Alberto,DICKSON, George J.
申请号：
EP17781644
公开号：
EP3443091A4
申请日:
2017.04.13
申请国别(地区):
EP
年份:
2019
代理人:
摘要：
The present disclosure relates to RNA interference (RNAi) reagents targeting PABPN1 for treatment of oculopharyngeal muscular dystrophy (OPMD), compositions comprising same, and use thereof to treat individuals suffering from OPMD or which are predisposed thereto.
