AKINC, AKIN,SORENSEN, BENNY,GARG, PUSHKAL,ROBBIE, GABRIEL
申请号:
CA3007014
公开号:
CA3007014A1
申请日:
2016.12.07
申请国别(地区):
CA
年份:
2017
代理人:
摘要:
The invention relates to iRNA, e.g., double stranded ribonucleic acid (dsRNA), compositions targeting the Serpinc1 gene, and methods of using such iRNA, e.g., dsRNA, compositions to inhibit expression of Serpinc1 and to treat subjects having a Serpinc1-associated disease, e.g., a bleeding disorder, such as a hemophilia.