補體組分C5 IRNA組合物及其應用方法

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专利权人:

Alnylam Pharmaceuticals; Inc.

发明人:

FITZGERALD, Kevin,BUTLER, James,BETTENCOURT, Brian,BORODOVSKY, Anna,KUCHIMANCHI, Satyanarayana,CHARISSE, Klaus,MANOHARAN, Muthiah,MAIER, Martin,RAJEEV, Kallanthottahil G.,FOSTER, Donald

申请号：

HK18111810

公开号：

HK1252501A1

申请日:

2018.09.14

申请国别(地区):

HK

年份:

2019

代理人:

摘要：

The invention relates to iRNA, e.g. , double-stranded ribonucleic acid (dsRNA), compositions targeting the complement component C5 gene, and methods of using such iRNA, e.g., dsRNA, compositions to inhibit expression of C5 and to treat subjects having a complement component C5-associated disease, e.g. , paroxysmal nocturnal hemoglobinuria.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/