Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones

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专利权人:

Amicus Therapeutics, Inc.

发明人:

Castelli Jeff,Lockhart David J.

申请号：

US201615213920

公开号：

US9999618(B2)

申请日:

2016.07.19

申请国别(地区):

美国

年份:

2018

代理人:

Servilla Whitney LLC

摘要：

The present invention provides dosing regimens for administering pharmacological chaperones to a subject in need thereof. The dosing regimens can be used to treat disorders caused by improper protein misfolding, such as lysosomal storage disorders.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/