Chemical molecules that inhibit the slicing mechanism for treating diseases resulting from splicing anomalies

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专利权人:

Florence Mahuteau-Betzer;David Grierson;Pierre Roux;Jamal Tazi

发明人:

Jamal Tazi,David Grierson,Florence Mahuteau-Betzer,Pierre Roux

申请号：

US12811931

公开号：

US08604063B2

申请日:

2009.01.12

申请国别(地区):

US

年份:

2013

代理人:

摘要：

The present invention relates to a compound of one of the formulas I to XXI； a pharmaceutical composition comprising at least one such compound； and the use of at least one such compound in preparing a drug to treat, in a subject, a genetic disease resulting from at least one splicing anomaly.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/