תכשירים ושיטות לטיפול במחלות

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专利权人:

UNIVERSITY OF FLORIDA RESEARCH FOUNDATION INC.

发明人:

申请号：

IL23629814

公开号：

IL236298D0

申请日:

2014.12.16

申请国别(地区):

IL

年份:

2015

代理人:

摘要：

The present invention provides compositions and methods of use pertaining to rAAV- mediated delivery of therapeutically effective molecules for treatment of diseases such as Pompe disease. These compositions in combination with various routes and methods of administration result in targeted expression of therapeutic molecules in specific organs, tissues and cells.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/