HIGH Katherine A.,YAZICIOGLU Mustafa N.,ANGUELA Xavier
申请号：
SI201431511
公开号：
SI3024498T1
申请日:
2014.07.22
申请国别(地区):
SI
年份:
2020
代理人:
摘要：
The invention relates to adeno-associated virus (AAV) serotype AAV-Rh74 and related AAV vectors, and AAV-Rh74 and related AAV vector mediated gene transfer methods and uses. In particular, AAV-Rh74 and related AAV vectors target polynucleotides to cells, tissues or organs for expression (transcription) of genes encoding therapeutic proteins and peptides, and polynucleotides that function as or are transcribed into inhibitory nucleic acid sequences.
