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OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
专利权人:
WAVE LIFE SCIENCES LTD.
发明人:
VARGEESE, Chandra,ZHONG, Zhong,IWAMOTO, Naoki,ZHANG, Jason Jingxin,DODART, Jean-Cosme,LIU, Yuanjing,KANDASAMY, Pachamuthu,DIVAKARAMENON, Sethumadhavan,LU, Genliang,MARAPPAN, Subramanian
申请号:
SG11202000274R
公开号:
SG11202000274RA
申请日:
2018.08.07
申请国别(地区):
SG
年份:
2020
代理人:
摘要:
INTERNATIONAL APPLICATION (19) World Intellectual Property Organization International Bureau PUBLISHED UNDER THE PATENT COOPERATION TREATY (PCT) IiiiionolivivivillEviiliololviiiilviviiEmolivimovois (10) International Publication Number WO 2019/032612 Al (43) International Publication Date 14 February 2019 (14.02.2019) WIPO I PCT (51) International Patent Classification: (72) Inventors; and A61K 31/711 (2006.01) A61K 31/7125 (2006.01) (71) Applicants (for US only): VARGEESE, Chandra A61K 31/712 (2006.01) C12N 15/113 (2010.01) [US/US]; c/o WAVE LIFE SCIENCES LTD., 733 Concord (21) International Application Number: PCT/US2018/045659 Avenue, Cambridge, Massachusetts 02138 (US). ZHONG, Zhong [US/US]; c/o WAVE LIFE SCIENCES LTD., 733 Concord Avenue, Cambridge, Massachusetts 02138 (US). IWAMOTO, Naoki [JP/US]; c/o WAVE LIFE (22) International Filing Date: SCIENCES LTD., 733 Concord Avenue, Cambridge, Mass- 07 August 2018 (07.08.2018) achusetts 02138 (US). ZHANG, Jason Jingxin [US/US]; (25) Filing Language: English c/o WAVE LIFE SCIENCES LTD., 733 Concord Avenue, Cambridge, Massachusetts 02138 (US). DODART, Jean- English (26) Publication Language: Cosme [US/US]; c/o WAVE LIFE SCIENCES LTD., 733 (30) Priority Data: Concord Avenue, Cambridge, Massachusetts 02138 (US). 62/542,778 08 August 2017 (08.08.2017) US LIU, Yuanjing [CN/US]; c/o WAVE LIFE SCIENCES LTD., 733 Concord Avenue, Cambridge, Massachusetts (71) Applicant: WAVE LIFE SCIENCES LTD. [SG/SG]; 7 02138 (US). KANDASAMY, Pachamuthu [CA/US]; c/ Straits View #12-00, Marina One East Tower, Singapore o WAVE LIFE SCIENCES LTD., 733 Concord Avenue, 018936 (SG). Cambridge, Massachusetts 02138 (US). DIVAKARA- (54) Title: OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF FIG. 4 mRNA Vi V3 V2 Pa Ioaical allele PGGGCC)30+ lb 2 34 5 6 7 8 91011 ViDet—E}Filia arefl—OH-Eli11-14-414 V3 Det -- EN - 00 - 4} - 04÷00 MUM Vi vs V2 Era min 81111111111111IM V2 13-EIHEHHHHO Pathological b V1 /Y3 + intronl ace Stabilized in tron 1 4 AS RNA Almi
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