Nippon Shinyaku Co., Ltd.;National Center of Neurology and Psychiatry
发明人:
申请号:
EP15810097.4
公开号:
EP3159409A4
申请日:
2015.06.16
申请国别(地区):
EP
年份:
2018
代理人:
摘要:
Provided is a drug that allows highly-efficient skipping of exon. The present invention provides an antisense oligomer wherein two or more unit oligomers targeting sequences that are neither consecutive nor overlap with each other in the same exon are connected.