THERAPEUTIC COMPOSITIONS OF ALPHA-L-IDURONIDASE, IDURONATE-2-SULFATASE, AND ALPHA-GALACTOSIDASE A AND METHODS OF USE THEREOF

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专利权人:

发明人:

申请号：

EP15858852.5

公开号：

EP3218000A2

申请日:

2015.11.10

申请国别(地区):

EP

年份:

2017

代理人:

摘要：

The present invention provides pharmaceutical compositions comprising an a blood brain barrier peptide and a human peptide, such as an alpha-L-iduronidase (IDUA) protein, an iduronate-2-sulfatase protein (IDS) protein, or an a galactosidase A protein (a-Gal A) protein. The invention further provides methods of use for treating Mucopolysaccharidosis type I (MPS I), including Hurler Syndrome, Hurler-Scheie Syndrome and Scheie Syndrome methods of use for treating Hunter syndrome and methods of use for treating Fabry disease.

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中国工程科技知识中心

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