Dosing Regimens for the Treatment of Lysosomal Storage Diseases Using Pharmacological Chaperones

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专利权人:

Amicus Therapeutics; Inc.

发明人:

Jeff Castelli,David J. Lockhart

申请号：

US16011075

公开号：

US20180360814A1

申请日:

2018.06.18

申请国别(地区):

US

年份:

2018

代理人:

摘要：

The present invention provides dosing regimens for administering pharmacological chaperones to a subject in need thereof. The dosing regimens can be used to treat disorders caused by improper protein misfolding, such as lysosomal storage disorders.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/