SAREPTA THERAPEUTICS; INC.;SAREPTA THERAPEUTICS, INC.;THE UNITED STATES OF AMERICA, AS REPRESENTED BY THE SECRETARY, DEPT. OF HEALTH AND HUMAN SERVICES;UNIVERSITY OF MARYLAND;THE PROGERIA RESEARCH FOUNDATION
发明人:
ERDOS, MICHAEL R.,COLLINS, FRANCIS S.,CAO, KAN,KOLE, RYSZARD,BESTWICK, RICHARD KEITH,GORDON, LESLIE B.
申请号：
CA3022303
公开号：
CA3022303A1
申请日:
2017.04.28
申请国别(地区):
CA
年份:
2017
代理人:
摘要：
Provided are LMNA-targeted antisense oligonucleotides for reducing expression of one or more aberrantly spliced LMNA mRNA isoforms that encode progerin.
