NATIONWIDE CHILDREN'S HOSPITAL INC.;NATIONWIDE CHILDRENS HOSPITAL INC.;OHIO STATE INNOVATION FOUNDATION
发明人:
KASPAR, BRIAN K.,FOUST, KEVIN
申请号：
CA3044291
公开号：
CA3044291A1
申请日:
2017.11.17
申请国别(地区):
CA
年份:
2018
代理人:
摘要：
Methods and materials for intrathecal delivery of recombinant Adeno-associated virus 9 (rAAV9) encoding Methyl-CpG binding protein 2 (MECP2) are provided. Use of the methods and materials is contemplated, for example, for the treatment of Rett syndrome.
