Compounds as modulators of a mutant CFTR protein and their use for treating diseases associated with CFTR protein malfunction

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专利权人:

Instytut Biochemii I Biofizyki Pan

发明人:

Odolczyk, Norbert,Zielenkiewicz, Piotr,Zorek, Grzegorz,Edelman, Aleksander,Tondelier, Danielle,Fritsch, Janine

申请号：

AU2015201410

公开号：

AU2015201410B2

申请日:

2015.03.18

申请国别(地区):

AU

年份:

2016

代理人:

摘要：

#$%^&*AU2015201410B220161103.pdf#####H:\rbr\Interwoven\NRPortbI\DCC\RBR\7513411 L.docx-3/03/2015 Abstract The present invention relates to novel protein modulators capable of altering function of the mutant CFTR protein and their use for treating diseases associated with CFTR protein malfunction. The invention provides compositions, pharmaceutical preparations and methods 5 of correcting the cellular alteration of a mutant CFTR protein wherein the CFTR mutation is a mutation AF508-CFTR, or another mutation of class II.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/