PASSINI, Marco, A.,SHIHABUDDIN, Lamya,CHENG, Seng, H.
申请号：
DK10772363
公开号：
DK2424991T3
申请日:
2010.04.27
申请国别(地区):
DK
年份:
2018
代理人:
摘要：
Compositions and methods for treating disorders affecting motor function, such as motor function affected by disease or injury to the brain and/or spinal cord, are disclosed. Also disclosed is a self-complementary adeno-associated virus vector for treating motor neuron disorders such as spinal muscular atrophy, amytrophic lateral sclerosis, spinal bulbar muscular atrophy, spinal cerebellar ataxia, primary lateral sclerosis, and traumatic spinal cord injury.
