MATERIALS AND METHODS FOR TREATMENT OF SEVERE COMBINED IMMUNODEFICIENCY (SCID) OR OMENN SYNDROME

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专利权人:

发明人:

申请号：

EP17716982.8

公开号：

EP3416689A1

申请日:

2017.02.17

申请国别(地区):

EP

年份:

2018

代理人:

摘要：

Materials and methods for treating a patient with severe combined immunodeficiency (SCID) or Omenn Syndrome, both ex vivo and in vivo, and materials and methods for editing to modulate the expression, function, or activity of an lnterleukin-7 receptor (IL7R) gene in a cell by genome editing.

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中国工程科技知识中心

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http://www.ckcest.cn/home/