CNS GENE DELIVERY USING PERIPHERAL ADMINISTRATION OF AAV VECTORS

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专利权人:

CENTRE NATIONAL DE LA RECHERCHE SCIENTIFIQUE

发明人:

MARTINE BARKATS

申请号：

PT08786331

公开号：

PT2185712T

申请日:

2008.07.22

申请国别(地区):

PT

年份:

2016

代理人:

摘要：

The present invention relates to compositions and methods for the delivery of therapeutic proteins to the CNS using recombinant AAV vectors. More specifically, the invention relates to compositions and methods for delivering proteins into the cerebrospinal fluid of mammalian subjects through peripheral administration of AAV vectors. The invention may be used to treat various disorders of the central nervous system, including degenerative diseases and motor neuron diseases.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/