Baylor College Of Medicine;Ionis Pharmaceuticals, Inc.
发明人:
申请号：
EP13809694.6
公开号：
EP2864479B1
申请日:
2013.06.25
申请国别(地区):
EP
年份:
2018
代理人:
摘要：
Certain embodiments are directed to methods and compounds for inhibiting UBE3A-ATS, the endogenous antisense transcript of ubiquitin protein ligase E3A (UBE3A). Such methods and compounds are useful for inducing expression of paternal UBE3A in cells and animals.
