University of Florida Research Foundation Incorporated
发明人:
Manuela Corti,Barry John Byrne
申请号：
US15568961
公开号：
US20180117178A1
申请日:
2016.04.23
申请国别(地区):
US
年份:
2018
代理人:
摘要：
Provided herein are nucleic acids, recombinant adeno-associated viral particles, compositions and methods related to treating Friedreich's ataxia. In some examples, the nucleic acids, recombinant adeno-associated viral particles, compositions and methods involve use of a FXN coding sequence, a truncated FXN 3′ UTR, and a promoter.
