600121 Discloses an adeno-associated virus (AAV) comprising an AAv9 capsid having a sequence identity of amino acids 1-736 of SEQ ID NO: 100 or a sequence having at least 95% identity therewith and a minigene having AAV inverted terminal repeats (ITRs) and a heterologous gene operably linked to regulatory sequences which direct its expression in a host cell. Also discloses capsid proteins within SEQ ID NO: 5.