Inhibitors of CACNA1A/ALPHA1A subunit internal ribosomal entry site (IRES) and methods of treating spinocerebellar ataxia type 6

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专利权人:

发明人:

Christopher M. Gomez,Xiaofei Du

申请号：

US15024492

公开号：

US10017765B2

申请日:

2014.07.02

申请国别(地区):

US

年份:

2018

代理人:

摘要：

The disclosure provides methods of treating polyglutamine diseases, e.g., spinocerebellar ataxia Type 6, in a subject, comprising administering to the subject an IRES inhibitor in an amount effective for treating the SCA6 in the subject. Also provided herein are the IRES inhibitors, and pharmaceutical compositions comprising the same.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/