Methods for the treatment of Danon disease and other disorders of autophagy
- 专利权人:
- The Regents of the University of California
- 发明人:
- Adler, Eric D.,Nelson, Bradley,Hashem, Sherin
- 申请号：
- AU2017209189
- 公开号：
- AU2017209189A1
- 申请日:
- 2017.01.19
- 申请国别(地区):
- AU
- 年份:
- 2018
- 代理人:
- 摘要：
- This disclosure provides gene therapy vectors comprising a polynucleotide encoding one or more isoforms of lysosome-associated membrane protein 2 (
- 来源网站：
- 中国工程科技知识中心
