COMBINED THERAPY FOR MUCOPOLYSACCHARIDOSIS TYPE VI (MAROTEAUX-LAMY-SYNDROME)

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专利权人:

FONDAZIONE TELETHON

发明人:

Alberto AURICCHIO,Marialuisa ALLIEGRO,Rita FERLA

申请号：

US16331358

公开号：

US20190343929A1

申请日:

2017.09.09

申请国别(地区):

US

年份:

2019

代理人:

摘要：

The present invention relates to a method for the treatment of MPS VI comprising administering an arylsulfatase B by gene therapy to a subject in need thereof, wherein said subject is administered with an arylsulfatase B enzyme replacement therapy (ERT) less frequently than once a week.

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